2.14 Nafamostat mesilate enhances antitumor effect of chemotherapy for pancreatic cancer.

T. Horiuchi1,2, H. Shiba1, Y. Shirai1,2, R. Iwase1,2, K. Haruki1, Y. Fujiwara1, K. Furukawa1, T. Uwagawa1, T. Ohashi2, K. Yanaga1  1The Jikei University School Of Medicine,Department Of Surgery,Tokyo, , Japan 2The Jikei University School Of Medicine,Department Of Gene Therapy, Research Center For Medical Science,Tokyo, , Japan

Introduction: ~Pancreatic cancer has a poor prognosis among visceral cancers, with an overall 5-year survival rate of around 5%. Currently, intravenous gemcitabine is a standard therapy for patient with advanced pancreatic cancer. Recently, gemcitabine plus nab-paclitaxel therapy was reported to be superior to gemcitabine alone in patients with advanced pancreatic cancer. However, the tumor resistance to chemotherapy is common and activation of nuclear factor-kappa B (NF-κB) is a key player in attenuation of anti-tumor effect of chemotherapy in pancreatic cancer. NF-κB is a transcription factor that plays an important role in the regulation of cell apoptosis, inflammation, and oncogenesis. Therefore, targeting downregulation of NF-κB activation is an important strategy to improve the efficacy of chemotherapy and outcome of patients with pancreatic cancer. We previously reported that nafamostat mesilate, a synthetic serine protease inhibitor, inhibited NF-κB activation and induced antitumor effects for pancreatic cancer. We hypothesized that nafamostat mesilate downregulates the activity of NF-κB and improves therapeutic outcome of pancreatic cancer. The purpose of this study is to prove that addition of nafamostat mesilate to gemcitabine and nab-paclitaxel enhances their antitumor effect against pancreatic cancer.

Methods: ~We assessed NF-κB activity and cell viability of human pancreatic cancer cell lines (PANC-1, MIA PaCa-2, ASPC-1) in the following five groups:  ① those treated with gemcitabine alone, ② gemcitabine and nab-paclitaxel,
③ nafamostat mesilate alone, ④ triple combination (gemcitabine, nab-paclitaxel and nafamostat mesilate), or ⑤ vehicle as control. In combination groups, the cells were treated with gemcitabine and nab-paclitaxel at the same time. In triple combination group, the cells were incubated with nafamostat mesilate at 3 hours before chemotherapy. Activation of NF-κB was evaluated by measuring nuclear localization of p65 protein.

Results:~Cell viability was assessed by the MTT assay. Cell viability in triple combination group was lower than that in gemcitabine plus nab-paclitaxel group (PANC 1: p<0.001, MIA PaCa-2: p=0.004, ASPC-1: p<0.001). The nuclear extracts were assessed using ELISA. NF-κB activity in gemcitabine plus nab-paclitaxel group was higher than that in control group, and NF-kB activity was significantly surpressed in nafamostat mesilate group and in tiple combination group compared with control group and gemcitabine plus nab-paclitaxel group, respectively (PANC-1: p<0.001, MIAPaCa-2: p<0.001, ASPC-1: p<0.001).

Conclusion:~Nafamostat mesilate significantly inhibited NF-κB activation and enhanced anti-tumor effect of gemcitabine plus nab-paclitaxel against human pancreatic cancer.